A型血友病市場:KOL的洞察
市場調查報告書
商品編碼
1728479

A型血友病市場:KOL的洞察

KOL Insight - Haemophilia A

出版日期: | 出版商: FirstWord Group | 英文 | 商品交期: 最快1-2個工作天內

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簡介目錄

本報告深入分析了血友病A的治療現狀,重點在於現有療法和創新研發管線產品。結合關鍵意見領袖的見解,對Hemlibra和Altuiiio等知名療法的療效、耐受性和劑量進行了評估。報告也探討了新型基因療法和雙特異性抗體的變革潛力。全面了解影響治療偏好的因素、新療法面臨的挑戰以及不斷發展的治療方案。

關鍵問題解答

  • 血友病A的第一線和二線治療方法有哪些?
  • 目前血友病A的治療方法在療效、耐受性和給藥便利性方面有何比較?
  • 研發管線療法必須具備哪些優點才能成為血友病A的首選治療方法?
  • 目前使用的血友病A療法和研發管線療法在未來的使用情況預計會發生哪些變化?
  • 為了有效競爭,研發產品必須達到哪些療效和耐受性終點?
  • 哪些研發產品最有前景?它們將如何影響當前的市場參與者?

領導品牌

  • Arhemo (concizumab)
  • Artsubio (efanesoctocog alfa)
  • ASC618 (CRISPR/Cas9編輯的hFVIII基因治療藥物)
  • BT200 (RNA調節劑/vWF抑制劑)
  • Dirloctocogene samoparvovec (SPK-8011)
  • Dirloctocogene fitelparvovec (PF-07055480/SB-525)
  • Hemlibra(艾美珠單抗)
  • Himpavzi(馬斯塔西單抗)
  • Inno8 (NNC0442-0344 A)
  • Mim8 (NNC0365-3769 A)
  • NEXT-007 (RG-6512/RO-7589655)
  • Pevoctocogene camaparvovec (DTX201)
  • Qfitlia(fitiran)
  • Roxavian(valoctocogene roxaparvovec)

部分參加專家名單

  • 血液學家、聖路易斯血友病中心主任英國倫敦聖托馬斯綜合護理中心
  • 美國紐約西奈山醫學中心血液學與腫瘤學系止血與血栓形成教授
  • 比利時布魯塞爾聖呂克大學血液學主任、醫學教授
  • 瑞典教學醫院醫學教授、血液學主任
  • 密西根州安娜堡密西根大學血友病和凝血障礙計畫兒科醫學主任、兒科和病理學教授
  • 加州洛杉磯南加州大學凱克醫學院兒科教授、止血和血栓形成計畫主任

方法

治療趨勢報告是透過對全球領先的關鍵意見領袖 (KOL) 就當前和未來治療前景進行深入訪談而得出的在關鍵疾病領域。我們根據嚴格的篩選標準精心挑選關鍵意見領袖 (KOL),這些標準包括全球聲譽、臨床專業知識以及在治療領域的影響力。每次訪談都附有精心設計的討論指南。這些指南由我們與關鍵意見領袖合作開發,並由行業專家進行同行評審,以確保所提問題全面且與當前市場動態相關。每份報告發布後,我們會持續進行12個月的市場監測,及時提供來自關鍵意見領袖的重大新聞事件、市場變化和市場發展動態的更新。

報告特色

FirstWord Reports 是值得信賴的行業領導者,專注於製藥領域,為生物製藥專業人士和決策者提供詳細且可操作的洞察。我們擁有深厚的行業知識,能夠為您提供相關且有價值的洞察,幫助您掌握新興趨勢,有​​效應對複雜挑戰。憑藉廣泛的研究以及來自頂尖專家和關鍵意見領袖的獨立、公正的見解,我們的報告能夠提供您所需的準確性和可靠性。獨家獨家訪談和數據,以及持續的市場監測,確保您全面了解市場動態。我們的報告涵蓋 40 多個活躍疾病領域,匯集醫生情報(包括 KOL 洞察和定量醫生調查),以及行業專家對醫療事務、數位醫療、銷售與市場營銷、市場准入及其他領域問題的看法,助您做出更明智的數據驅動決策,在快速變化的行業中保持競爭力。

簡介目錄

This report offers a detailed analysis of the haemophilia A treatment landscape, highlighting both current therapies and innovative pipeline products. Insights from leading key opinion leaders assess the efficacy, tolerability, and administration of prominent treatments like Hemlibra and Altuviiio. This report also explores the transformative potential of emerging gene therapies and bispecific antibodies. Gain a comprehensive understanding of the factors influencing treatment preferences, the challenges new therapies face, and the evolving treatment algorithms.

Key Questions Answered:

  • 1. What are the preferred first-line and subsequent-line treatments for haemophilia A, and why?
  • 2. How do current haemophilia A treatments compare in terms of efficacy, tolerability, and ease of administration?
  • 3. What must pipeline therapies demonstrate to become the treatment of choice in haemophilia A?
  • 4. How is the use of current and pipeline haemophilia A products expected to change in the future?
  • 5. What efficacy and tolerability endpoints must pipeline products achieve to compete effectively?
  • 6. Which pipeline products are most promising, and how will they impact current market players?

Key Brands:

  • Alhemo (concizumab)
  • Altuviiio (efanesoctocog alfa)
  • ASC618 (CRISPR/Cas9-edited hFVIII gene therapy)
  • BT200 (RNA modulator/vWF inhibitor)
  • Dirloctocogene samoparvovec (SPK-8011)
  • Giroctocogene fitelparvovec (PF-07055480/SB-525)
  • Hemlibra (emicizumab)
  • Hympavzi (marstacimab)
  • Inno 8 (NNC0442-0344 A)
  • Mim8 (NNC0365-3769 A)
  • NXT-007 (RG-6512/RO-7589655)
  • Peboctocogene camaparvovec (DTX201)
  • Qfitlia (fitusiran)
  • Roctavian (valoctocogene roxaparvovec)

Partial List of Participating Experts:

  • Consultant Haematologist, Haemophilia Centre Director, St Thomas' Comprehensive Care Centre, London, UK
  • Professor of Hemostasis and Thrombosis, Division of Hematology and Medical Oncology, Mount Sinai Medical Center, New York, NY
  • Professor of Medicine, Chef de Service - Service d'Hematologie chez Cliniques Universitaires Saint-Luc, Brussels, Belgium
  • Professor of Medicine, Director of Haematology at a teaching hospital, Sweden
  • Professor of Pediatrics and Pathology, Pediatric Medical Director, Hemophilia and Coagulation Disorders Program, University of Michigan, Ann Arbor, MI
  • Professor of Pediatrics, Director, Hemostasis and Thrombosis Program, Keck School of Medicine of USC, Los Angeles, CA

Methodology:

Therapy Trend reports are developed through in-depth interviews with the world's foremost Key Opinion Leaders (KOLs) on the current and future treatment landscapes in major disease areas. KOLs are carefully selected based on strict screening criteria, including their global reputation, clinical expertise, and influence within their therapeutic area. Each interview is guided by a meticulously crafted discussion guide. These guides are developed in collaboration with KOLs and peer-reviewed by industry experts to ensure that the questions are comprehensive and pertinent to current market dynamics. Through continuous market monitoring over a 12-month period following the publication of each report, we provide timely updates from KOLs on key news events, market shifts, and clinical developments.

What makes our reports different?

FirstWord Reports, a trusted industry leader with an exclusive focus on the pharmaceutical sector, delivers in-depth, actionable insights for biopharma professionals and decision-makers. Our deep industry knowledge enables us to provide relevant and valuable insights that help you identify emerging trends and navigate complex challenges effectively. Backed by extensive research and independent, impartial insights from leading experts and KOLs, our reports deliver the accuracy and reliability you need. With exclusive access to interviews and data unavailable elsewhere, along with ongoing market monitoring, we give you a comprehensive view of market dynamics. Covering over 40 dynamic disease areas and providing physician intelligence, including KOL insights and quantitative physician surveys, as well as industry expert views on issues in medical affairs, digital health, sales & marketing, market access, and other areas, our reports empower you to make smarter, data-driven decisions and maintain a competitive edge in a fast-moving industry.