罕見血友病因素市場 - 全球產業規模、佔有率、趨勢、機會和預測，按治療、類型、地區和競爭細分，2020-2030 年預測

2024 年全球罕見血友病因素市場價值為 3.2425 億美元，預計到 2030 年將達到 4.7514 億美元，預測期內複合年成長率為 6.58%。全球罕見血友病因素市場是廣泛醫療保健產業中一個充滿活力且至關重要的領域，專注於滿足患有罕見血友病患者的獨特需求。血友病是一種罕見的遺傳性疾病，其特徵是缺乏或缺乏特定的凝血因子，主要是因子 VIII（血友病 A）和因子 IX（血友病 B）。然而，還有更罕見的血友病，是由其他凝血因子缺乏引起的，包括因子 I、V、VII、X、XI 和 XIII。這些罕見的血友病變異在診斷、治療和患者護理方面帶來了獨特的挑戰。

罕見血友病因子市場涵蓋一系列專門針對與這些罕見凝血因子疾病相關的特定缺陷的產品和療法。這些治療旨在取代缺失的凝血因子或增強患者現有凝血因子的功能。近年來，創新療法的開發取得了重大進展，其中包括基因療法，預計將為患有罕見血友病因素的患者提供長期緩解。

市場的成長受到多種因素的推動，包括由於診斷和認知的提高而導致的罕見血友病因素疾病的患病率不斷增加、發展中國家醫療保健基礎設施的擴大，以及旨在改善治療方案的持續研發努力。此外，製藥公司、研究機構和患者權益團體之間的合作與夥伴關係也加速了該領域的進步。

主要市場促進因素

盛行率上升和診斷水準提高

主要市場挑戰

治療費用高昂

主要市場趨勢

基因治療的突破

目錄

第 1 章：產品概述

第 2 章：研究方法

第 3 章：執行摘要

第 4 章：全球罕見血友病因素市場展望

• 市場規模和預測
  • 按價值
• 市場佔有率和預測
  • 依治療方法（因子濃縮物、新鮮冷凍血漿、冷沉澱物、其他）
  • 依類型（因子 I、因子 II、因子 V、因子 VII、因子 X、因子 XI、因子 XIII）
  • 按地區
  • 按公司分類（2024）
• 市場地圖
  • 按治療
  • 按類型
  • 按地區

第 5 章：亞太地區罕見血友病因素市場展望

• 市場規模和預測
  • 按價值
• 市場佔有率和預測
  • 按治療
  • 按類型
  • 按國家
• 亞太地區：國家分析
  • 中國
  • 印度
  • 澳洲
  • 日本
  • 韓國

第 6 章：歐洲罕見血友病因素市場展望

• 市場規模和預測
• 市場佔有率和預測
• 歐洲：國家分析
  • 德國
  • 西班牙
  • 義大利
  • 英國

第 7 章：北美罕見血友病因素市場展望

• 市場規模和預測
• 市場佔有率和預測
• 北美：國家分析
  • 墨西哥
  • 加拿大

第 8 章：南美洲罕見血友病因素市場展望

• 市場規模和預測
• 市場佔有率和預測
• 南美洲：國家分析
  • 阿根廷
  • 哥倫比亞

第 9 章：中東和非洲罕見血友病因素市場展望

• 市場規模和預測
• 市場佔有率和預測
• MEA：國家分析
  • 沙烏地阿拉伯
  • 阿拉伯聯合大公國
  • 埃及

第 10 章：市場動態

• 驅動程式
• 挑戰

第 11 章：市場趨勢與發展

• 最新動態
• 治療啟動
• 合併與收購

第 12 章：全球罕見血友病因素市場：SWOT 分析

第 13 章：波特五力分析

• 產業競爭
• 新進入者的潛力
• 供應商的力量
• 顧客的力量
• 替代產品的威脅

第 14 章：競爭格局

• Novo Nordisk A/S
• Biogen
• Bayer AG
• Pfizer, Inc.
• Shire Pharmaceuticals
• Baxalta (Baxter Healthcare)
• CSL Behring
• Bio Products Laboratory Ltd.
• Takeda Pharmaceutical Co. Ltd.
• Alexion Pharmaceuticals, Inc.

第 15 章：策略建議

第16章調查會社について,免責事項

Global Rare Hemophilia Factors Market was valued at USD 324.25 million in 2024 and is expected to reach USD 475.14 million by 2030 with a CAGR of 6.58% during the forecast period. The Global Rare Hemophilia Factors Market is a dynamic and vital sector within the broader healthcare industry, focused on addressing the unique needs of individuals suffering from rare forms of hemophilia. Hemophilia is a rare genetic disorder characterized by the absence or deficiency of specific blood clotting factors, primarily Factor VIII (hemophilia A) and Factor IX (hemophilia B). However, there are even rarer forms of hemophilia that result from deficiencies in other clotting factors, including Factors I, V, VII, X, XI, and XIII. These rare hemophilia variants present distinct challenges in terms of diagnosis, treatment, and patient care.

The market for rare hemophilia factors encompasses a range of products and therapies tailored to address the specific deficiencies associated with these rare clotting factor disorders. These treatments are designed to either replace the missing clotting factors or enhance the function of the patient's existing clotting factors. In recent years, there have been significant advancements in the development of innovative therapies, including gene therapy, which holds promise for long-term relief for individuals with rare hemophilia factors.

The market's growth is driven by several factors, including the increasing prevalence of rare hemophilia factor disorders due to improved diagnosis and awareness, the expansion of healthcare infrastructure in developing countries, and ongoing research and development efforts aimed at improving treatment options. Additionally, collaborations and partnerships between pharmaceutical companies, research institutions, and patient advocacy groups have accelerated progress in the field.

Key Market Drivers

Rising Prevalence and Improved Diagnosis

Rising prevalence and improved diagnosis are among the foremost factors propelling the growth of the Global Rare Hemophilia Factors Market. Historically, patients with rare hemophilia factor deficiencies often faced delayed or misdiagnoses due to the complexities and the rarity of these disorders. However, in recent years, there has been a significant shift in the healthcare landscape with enhanced awareness, better diagnostic tools, and more comprehensive genetic testing.

The increasing prevalence of rare hemophilia factor deficiencies can be attributed, in part, to improved diagnosis. As healthcare professionals become more knowledgeable about these fewer common forms of hemophilia, more patients are correctly identified and diagnosed. This growing awareness, often fostered by patient advocacy groups, has led to a surge in demand for specialized therapies and treatments tailored to these unique clotting factor disorders. This, in turn, fuels the market by creating a larger patient pool seeking appropriate care.

Advancements in diagnostic technologies, particularly genetic testing, have been pivotal in this context. These tests enable healthcare providers to pinpoint the exact clotting factor deficiency and its genetic basis, allowing for precise and early diagnoses. Such early diagnosis is crucial because it enables timely intervention and personalized treatment strategies, significantly improving patient outcomes. Patients who were once left undiagnosed or misdiagnosed can now receive tailored care, leading to a better quality of life.

Furthermore, as the prevalence of rare hemophilia factor disorders becomes more apparent, healthcare systems worldwide are recognizing the importance of addressing these conditions and allocating resources to support affected individuals. This commitment is fostering a more patient-centric approach in healthcare, driving the development of novel therapies and treatment options.

Key Market Challenges

High Treatment Costs

The Global Rare Hemophilia Factors Market has made significant strides in addressing the unique needs of individuals with rare clotting factor deficiencies. While advancements in therapies have offered new hope to these patients, a pervasive challenge looms large - the high cost of treatment. The exorbitant price of specialized therapies designed for rare hemophilia factors is a key obstacle in achieving equitable access and comprehensive care for affected individuals.

Rare hemophilia factor deficiencies encompass various disorders that result from the deficiency of clotting factors other than the commonly known Factors VIII (hemophilia A) and IX (hemophilia B). These conditions, which include deficiencies in Factors I, V, VII, X, XI, and XIII, present unique challenges in diagnosis and management. As a result, specialized treatments are required, which are often considerably more expensive than traditional clotting factor replacement therapies.

The high treatment costs can be a significant financial burden for both patients and healthcare systems. For patients, it can lead to personal financial strain, jeopardizing their access to the critical care they need. In many cases, individuals with rare hemophilia factor deficiencies find themselves grappling with out-of-pocket expenses that are simply unaffordable. This financial burden can result in treatment non-compliance, reduced quality of life, and overall health complications.

Key Market Trends

Gene Therapy Breakthroughs

Gene therapy breakthroughs have emerged as a powerful driving force in the Global Rare Hemophilia Factors Market. Rare hemophilia factor deficiencies, resulting from the absence or dysfunction of specific clotting factors, have long presented significant challenges in terms of treatment. However, recent breakthroughs in gene therapy are fundamentally transforming the landscape of care for individuals with these conditions, offering newfound hope, improved outcomes, and a promising shift away from lifelong clotting factor replacement therapy.

Gene therapy for rare hemophilia factors involves the introduction of a functional copy of the deficient clotting factor gene into the patient's cells, addressing the root genetic cause of the deficiency. This innovative approach has yielded remarkable results, offering potential cures rather than just symptom management. Clinical trials have demonstrated the safety and efficacy of gene therapy in treating rare hemophilia, showing that it can lead to sustained production of the deficient clotting factor, reducing or eliminating the need for regular infusions of clotting factor concentrates.

Key Market Players

• Novo Nordisk A/S
• Biogen
• Bayer AG
• Pfizer, Inc.
• Shire Pharmaceuticals
• Baxalta (Baxter Healthcare)
• CSL Behring
• Bio Products Laboratory Ltd.
• Takeda Pharmaceutical Co. Ltd.
• Alexion Pharmaceuticals, Inc.

Report Scope:

In this report, the Global Rare Hemophilia Factors Market has been segmented into the following categories, in addition to the industry trends which have also been detailed below:

Rare Hemophilia Factors Market, By Treatment:

• Factor Concentrates
• Fresh Frozen Plasma
• Cryoprecipitate
• Others

Rare Hemophilia Factors Market, By Type:

• Factor I
• Factor II
• Factor V
• Factor VII
• Factor X
• Factor XI
• Factor XIII

Rare Hemophilia Factors Market, By Region:

• North America
  • United States
  • Canada
  • Mexico
• Europe
  • France
  • United Kingdom
  • Italy
  • Germany
  • Spain
• Asia-Pacific
  • China
  • India
  • Japan
  • Australia
  • South Korea
• South America
  • Brazil
  • Argentina
  • Colombia
• Middle East & Africa
  • South Africa
  • Saudi Arabia
  • UAE
  • Egypt

Competitive Landscape

Company Profiles: Detailed analysis of the major companies present in the Global Rare Hemophilia Factors Market.

Available Customizations:

Global Rare Hemophilia Factors Market report with the given market data, TechSci Research offers customizations according to a company's specific needs. The following customization options are available for the report:

Company Information

• Detailed analysis and profiling of additional market players (up to five).

Table of Contents

1. Product Overview

• 1.1. Market Definition
• 1.2. Scope of the Market
  • 1.2.1. Markets Covered
  • 1.2.2. Years Considered for Study
  • 1.2.3. Key Market Segmentations

2. Research Methodology

• 2.1. Objective of the Study
• 2.2. Baseline Methodology
• 2.3. Key Industry Partners
• 2.4. Major Association and Secondary Sources
• 2.5. Forecasting Methodology
• 2.6. Data Triangulation & Validation
• 2.7. Assumptions and Limitations

3. Executive Summary

• 3.1. Overview of the Market
• 3.2. Overview of Key Market Segmentations
• 3.3. Overview of Key Market Players
• 3.4. Overview of Key Regions/Countries
• 3.5. Overview of Market Drivers, Challenges, Trends

4. Global Rare Hemophilia Factors Market Outlook

• 4.1. Market Size & Forecast
  • 4.1.1. By Value
• 4.2. Market Share & Forecast
  • 4.2.1. By Treatment (Factor Concentrates, Fresh Frozen Plasma, Cryoprecipitate, Others)
  • 4.2.2. By Type (Factor I, Factor II, Factor V, Factor VII, Factor X, Factor XI, Factor XIII)
  • 4.2.3. By Region
  • 4.2.4. By Company (2024)
• 4.3. Market Map
  • 4.3.1. By Treatment
  • 4.3.2. By Type
  • 4.3.3. By Region

5. Asia Pacific Rare Hemophilia Factors Market Outlook

• 5.1. Market Size & Forecast
  • 5.1.1. By Value
• 5.2. Market Share & Forecast
  • 5.2.1. By Treatment
  • 5.2.2. By Type
  • 5.2.3. By Country
• 5.3. Asia Pacific: Country Analysis
  • 5.3.1. China Rare Hemophilia Factors Market Outlook
    • 5.3.1.1. Market Size & Forecast
      • 5.3.1.1.1. By Value
    • 5.3.1.2. Market Share & Forecast
      • 5.3.1.2.1. By Treatment
      • 5.3.1.2.2. By Type
  • 5.3.2. India Rare Hemophilia Factors Market Outlook
    • 5.3.2.1. Market Size & Forecast
      • 5.3.2.1.1. By Value
    • 5.3.2.2. Market Share & Forecast
      • 5.3.2.2.1. By Treatment
      • 5.3.2.2.2. By Type
  • 5.3.3. Australia Rare Hemophilia Factors Market Outlook
    • 5.3.3.1. Market Size & Forecast
      • 5.3.3.1.1. By Value
    • 5.3.3.2. Market Share & Forecast
      • 5.3.3.2.1. By Treatment
      • 5.3.3.2.2. By Type
  • 5.3.4. Japan Rare Hemophilia Factors Market Outlook
    • 5.3.4.1. Market Size & Forecast
      • 5.3.4.1.1. By Value
    • 5.3.4.2. Market Share & Forecast
      • 5.3.4.2.1. By Treatment
      • 5.3.4.2.2. By Type
  • 5.3.5. South Korea Rare Hemophilia Factors Market Outlook
    • 5.3.5.1. Market Size & Forecast
      • 5.3.5.1.1. By Value
    • 5.3.5.2. Market Share & Forecast
      • 5.3.5.2.1. By Treatment
      • 5.3.5.2.2. By Type

6. Europe Rare Hemophilia Factors Market Outlook

• 6.1. Market Size & Forecast
  • 6.1.1. By Value
• 6.2. Market Share & Forecast
  • 6.2.1. By Treatment
  • 6.2.2. By Type
  • 6.2.3. By Country
• 6.3. Europe: Country Analysis
  • 6.3.1. France Rare Hemophilia Factors Market Outlook
    • 6.3.1.1. Market Size & Forecast
      • 6.3.1.1.1. By Value
    • 6.3.1.2. Market Share & Forecast
      • 6.3.1.2.1. By Treatment
      • 6.3.1.2.2. By Type
  • 6.3.2. Germany Rare Hemophilia Factors Market Outlook
    • 6.3.2.1. Market Size & Forecast
      • 6.3.2.1.1. By Value
    • 6.3.2.2. Market Share & Forecast
      • 6.3.2.2.1. By Treatment
      • 6.3.2.2.2. By Type
  • 6.3.3. Spain Rare Hemophilia Factors Market Outlook
    • 6.3.3.1. Market Size & Forecast
      • 6.3.3.1.1. By Value
    • 6.3.3.2. Market Share & Forecast
      • 6.3.3.2.1. By Treatment
      • 6.3.3.2.2. By Type
  • 6.3.4. Italy Rare Hemophilia Factors Market Outlook
    • 6.3.4.1. Market Size & Forecast
      • 6.3.4.1.1. By Value
    • 6.3.4.2. Market Share & Forecast
      • 6.3.4.2.1. By Treatment
      • 6.3.4.2.2. By Type
  • 6.3.5. United Kingdom Rare Hemophilia Factors Market Outlook
    • 6.3.5.1. Market Size & Forecast
      • 6.3.5.1.1. By Value
    • 6.3.5.2. Market Share & Forecast
      • 6.3.5.2.1. By Treatment
      • 6.3.5.2.2. By Type

7. North America Rare Hemophilia Factors Market Outlook

• 7.1. Market Size & Forecast
  • 7.1.1. By Value
• 7.2. Market Share & Forecast
  • 7.2.1. By Treatment
  • 7.2.2. By Type
  • 7.2.3. By Country
• 7.3. North America: Country Analysis
  • 7.3.1. United States Rare Hemophilia Factors Market Outlook
    • 7.3.1.1. Market Size & Forecast
      • 7.3.1.1.1. By Value
    • 7.3.1.2. Market Share & Forecast
      • 7.3.1.2.1. By Treatment
      • 7.3.1.2.2. By Type
  • 7.3.2. Mexico Rare Hemophilia Factors Market Outlook
    • 7.3.2.1. Market Size & Forecast
      • 7.3.2.1.1. By Value
    • 7.3.2.2. Market Share & Forecast
      • 7.3.2.2.1. By Treatment
      • 7.3.2.2.2. By Type
  • 7.3.3. Canada Rare Hemophilia Factors Market Outlook
    • 7.3.3.1. Market Size & Forecast
      • 7.3.3.1.1. By Value
    • 7.3.3.2. Market Share & Forecast
      • 7.3.3.2.1. By Treatment
      • 7.3.3.2.2. By Type

8. South America Rare Hemophilia Factors Market Outlook

• 8.1. Market Size & Forecast
  • 8.1.1. By Value
• 8.2. Market Share & Forecast
  • 8.2.1. By Treatment
  • 8.2.2. By Type
  • 8.2.3. By Country
• 8.3. South America: Country Analysis
  • 8.3.1. Brazil Rare Hemophilia Factors Market Outlook
    • 8.3.1.1. Market Size & Forecast
      • 8.3.1.1.1. By Value
    • 8.3.1.2. Market Share & Forecast
      • 8.3.1.2.1. By Treatment
      • 8.3.1.2.2. By Type
  • 8.3.2. Argentina Rare Hemophilia Factors Market Outlook
    • 8.3.2.1. Market Size & Forecast
      • 8.3.2.1.1. By Value
    • 8.3.2.2. Market Share & Forecast
      • 8.3.2.2.1. By Treatment
      • 8.3.2.2.2. By Type
  • 8.3.3. Colombia Rare Hemophilia Factors Market Outlook
    • 8.3.3.1. Market Size & Forecast
      • 8.3.3.1.1. By Value
    • 8.3.3.2. Market Share & Forecast
      • 8.3.3.2.1. By Treatment
      • 8.3.3.2.2. By Type

9. Middle East and Africa Rare Hemophilia Factors Market Outlook

• 9.1. Market Size & Forecast
  • 9.1.1. By Value
• 9.2. Market Share & Forecast
  • 9.2.1. By Treatment
  • 9.2.2. By Type
  • 9.2.3. By Country
• 9.3. MEA: Country Analysis
  • 9.3.1. South Africa Rare Hemophilia Factors Market Outlook
    • 9.3.1.1. Market Size & Forecast
      • 9.3.1.1.1. By Value
    • 9.3.1.2. Market Share & Forecast
      • 9.3.1.2.1. By Treatment
      • 9.3.1.2.2. By Type
  • 9.3.2. Saudi Arabia Rare Hemophilia Factors Market Outlook
    • 9.3.2.1. Market Size & Forecast
      • 9.3.2.1.1. By Value
    • 9.3.2.2. Market Share & Forecast
      • 9.3.2.2.1. By Treatment
      • 9.3.2.2.2. By Type
  • 9.3.3. UAE Rare Hemophilia Factors Market Outlook
    • 9.3.3.1. Market Size & Forecast
      • 9.3.3.1.1. By Value
    • 9.3.3.2. Market Share & Forecast
      • 9.3.3.2.1. By Treatment
      • 9.3.3.2.2. By Type
  • 9.3.4. Egypt Rare Hemophilia Factors Market Outlook
    • 9.3.4.1. Market Size & Forecast
      • 9.3.4.1.1. By Value
    • 9.3.4.2. Market Share & Forecast
      • 9.3.4.2.1. By Treatment
      • 9.3.4.2.2. By Type

10. Market Dynamics

• 10.1. Drivers
• 10.2. Challenges

11. Market Trends & Developments

• 11.1. Recent Developments
• 11.2. Treatment Launches
• 11.3. Mergers & Acquisitions

12. Global Rare Hemophilia Factors Market: SWOT Analysis

13. Porter's Five Forces Analysis

• 13.1. Competition in the Industry
• 13.2. Potential of New Entrants
• 13.3. Power of Suppliers
• 13.4. Power of Customers
• 13.5. Threat of Substitute Product

14. Competitive Landscape

• 14.1. Novo Nordisk A/S
  • 14.1.1. Business Overview
  • 14.1.2. Company Snapshot
  • 14.1.3. Products & Services
  • 14.1.4. Financials (In case of listed)
  • 14.1.5. Recent Developments
  • 14.1.6. Key Personnel Details
  • 14.1.7. SWOT Analysis
• 14.2. Biogen
• 14.3. Bayer AG
• 14.4. Pfizer, Inc.
• 14.5. Shire Pharmaceuticals
• 14.6. Baxalta (Baxter Healthcare)
• 14.7. CSL Behring
• 14.8. Bio Products Laboratory Ltd.
• 14.9. Takeda Pharmaceutical Co. Ltd.
• 14.10. Alexion Pharmaceuticals, Inc.

15. Strategic Recommendations

16. About Us & Disclaimer