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市場調查報告書
商品編碼
1786775

溶小體儲積症治療的全球市場,規模,佔有率,趨勢,產業分析報告:各疾病類型,各治療類型,各終端用戶,各地區 - 市場預測,2025年~2034年

Lysosomal Storage Disease Treatment Market Size, Share, Trends, & Industry Analysis Report By Disease Type, By Type of Therapy, By End User, and By Region - Market Forecast, 2025-2034

出版日期: | 出版商: Polaris Market Research | 英文 129 Pages | 商品交期: 最快1-2個工作天內

價格

根據 Polaris Market Research 的最新研究,溶小體貯積症治療市場預計到 2034 年將達到 68 億美元。本研究報告深入分析了當前的市場動態,並分析了未來的市場成長。

隨著製藥公司和研發機構開發針對罕見遺傳疾病的新療法,溶小體貯積症治療市場正在穩步發展。認知度的提高、患者權益的增強以及支持性監管框架的完善,有助於加快藥物審批,並改善創新療法的可及性。

生物技術和個人化醫療投資的不斷增加,正在將市場重點從對症治療轉向長期疾病管理和潛在治癒方法的開發。這一發展反映了人們對改善患者預後以及為戈謝氏症、法布瑞氏症和龐貝氏症等疾病提供更有效、更有針對性的治療方案的強烈追求。

溶小體貯積症治療市場報告重點

按疾病類型劃分,戈謝氏症將在2024年佔市場主導地位,這得益於其在全球的廣泛流行和成熟的治療生態系統。

按治療類型劃分,酵素替代療法 (ERT) 細分市場在2024年佔市場主導地位,這得益於其在各種溶酶體貯積症治療中的應用日益廣泛。

依最終用戶劃分,提供酵素替代療法和幹細胞治療等專業介入措施的醫院細分市場在2024年佔市場主導地位。

受強勁的…推動,北美佔了全球溶小體貯積症治療市場的大部分佔有率,2024年市場佔有率達到36.98%。生物技術和製藥公司正在開發治療罕見遺傳疾病的藥物。

亞太地區佔了 6.13% 的市場佔有率,這得益於醫療保健基礎設施的持續改善和先進診斷能力的普及。

全球主要市場參與者包括 Alexion Pharmaceuticals, Inc.、Amicus Therapeutics, Inc.、BioMarin Pharmaceutical Inc.、禮來公司、強生公司(Actelion Pharmaceuticals Ltd.)、默克公司、諾華公司、輝田公司、賽諾菲公司(健贊公司)、Sigilon Therapeutics, Inc. S.p.A.、Orphazyme A/S、Protalix BioTherapeutics, Inc. 和 Ultragenyx Pharmaceutical Inc.

目錄

第1章 簡介

第2章 摘要整理

第3章 調查手法

第4章 全球溶小體儲積症治療市場洞察

  • 市場概述
  • 溶小體儲積症治療市場動態
    • 促進因素和機會
      • 罕見遺傳疾病發生率上升
      • 酵素替代療法 (ERT) 的進展
    • 限制與課題
      • 治療費用高且報銷有限
  • PESTEL分析
  • 溶小體儲積症治療市場趨勢
  • 價值鏈分析

第5章 全球溶小體儲積症治療市場:各疾病類型

  • 主要調查結果
  • 簡介
  • 高雪氏症
  • 法布瑞氏症
  • 龐貝氏症
  • 黏多醣症
  • 其他

第6章 全球溶小體儲積症治療市場:各治療類型

  • 主要調查結果
  • 簡介
  • 酵素補充療法
  • 幹細胞療法
  • 基材還原療法
  • 其他

第7章 全球溶小體儲積症治療市場:各終端用戶

  • 主要調查結果
  • 簡介
  • 醫院
  • 診所
  • 其他

第8章 全球溶小體儲積症治療市場:各地區

  • 主要調查結果
  • 簡介
    • 溶小體儲積症治療市場評估:各地區,2020-2034年
  • 北美
    • 北美:各疾病類型,2020~2034年
    • 北美:各治療類型,2020年~2034年
    • 北美:各終端用戶,2020~2034年
    • 美國
    • 加拿大
  • 歐洲
    • 歐洲:各疾病類型,2020~2034年
    • 歐洲:各治療類型,2020~2034年
    • 歐洲:各終端用戶,2020~2034年
    • 英國
    • 法國
    • 德國
    • 義大利
    • 西班牙
    • 荷蘭
    • 俄羅斯
    • 其他歐洲
  • 亞太地區
    • 亞太地區:疾病各類型,2020~2034年
    • 亞太地區:各治療類型,2020年~2034年
    • 亞太地區:各終端用戶,2020~2034年
    • 中國
    • 印度
    • 馬來西亞
    • 日本
    • 印尼
    • 韓國
    • 澳洲
    • 其他亞太地區
  • 中東·非洲
    • 中東·非洲:疾病各類型,2020~2034年
    • 中東·非洲:各治療類型,2020~2034年
    • 中東·非洲:各終端用戶,2020~2034年
    • 沙烏地阿拉伯
    • 阿拉伯聯合大公國
    • 以色列
    • 南非
    • 其他中東·非洲
  • 南美
    • 南美:疾病各類型,2020-2034年
    • 南美:各治療類型,2020-2034年
    • 南美:各終端用戶,2020~2034年
    • 墨西哥
    • 巴西
    • 阿根廷
    • 其他南美國家

第9章 競爭情形

  • 擴大和收購的分析
    • 擴大
    • 收購
  • 聯盟/合作/協定/公開

第10章 企業簡介

  • Alexion Pharmaceuticals, Inc.
  • Amicus Therapeutics, Inc.
  • BioMarin Pharmaceutical Inc.
  • Eli Lilly and Company
  • Johnson & Johnson(Actelion Pharmaceuticals Ltd.)
  • Merck & Co., Inc.
  • Novartis AG
  • Pfizer Inc.
  • Sanofi(Genzyme Corporation)
  • Sigilon Therapeutics, Inc.
  • Takeda Pharmaceutical Company Limited(Shire Plc)
  • Chiesi Farmaceutici S.p.A.
Product Code: PM6066

The lysosomal storage disease treatment market size is expected to reach USD 6.80 Billion by 2034, according to a new study by Polaris Market Research. The report "Lysosomal Storage Disease Treatment Market Size, Share, Trends, & Industry Analysis Report By Disease Type (Gaucher's Diseases, Fabry Diseases, Pompe's Syndrome, Mucopolysaccharidosis, and Others), By Type of Therapy, By End User, and By Region - Market Forecast, 2025-2034" gives a detailed insight into current market dynamics and provides analysis on future market growth.

The lysosomal storage disease (LSD) treatment market is witnessing steady progress as pharmaceutical companies and research institutions develop new therapies aimed at addressing rare genetic disorders. Growing awareness, increasing patient advocacy, and supportive regulatory frameworks are helping accelerate drug approvals and improve access to innovative treatments.

Rising investments in biotechnology and personalized medicine are shifting the market focus beyond symptom control toward long-term disease management and the development of potential cures. This evolution reflects a strong push toward improving patient outcomes and delivering more effective, targeted therapies for conditions such as Gaucher disease, Fabry disease, and Pompe disease.

Lysosomal Storage Disease Treatment Market Report Highlights

Based on disease type, gaucher's disease segment dominated the market in 2024, driven by its wider global prevalence and the presence of an established therapeutic ecosystem.

In terms of type of therapy, the enzyme replacement therapy (ERT) segment dominated the market in 2024. This is driven by the increasing adoption in managing various lysosomal storage disorders.

In terms of end user, the hospital segment dominated the market in 2024, attributed to delivery of specialized interventions such as enzyme replacement therapies and stem cell-based procedures.

North America accounted for the majority share of 36.98 in the global lysosomal storage disease treatment market in 2024, due to the strong presence of biotech and pharmaceutical firms advancing treatments for rare genetic conditions.

Asia Pacific held 6.13% market share, owing to ongoing improvements in healthcare infrastructure and access to advanced diagnostic capabilities.

A few global key market players include Alexion Pharmaceuticals, Inc., Amicus Therapeutics, Inc., BioMarin Pharmaceutical Inc., Eli Lilly and Company, Johnson & Johnson (Actelion Pharmaceuticals Ltd.), Merck & Co., Inc., Novartis AG, Pfizer Inc., Sanofi (Genzyme Corporation), Sigilon Therapeutics, Inc., Takeda Pharmaceutical Company Limited (Shire Plc), Chiesi Farmaceutici S.p.A., Orphazyme A/S, Protalix BioTherapeutics, Inc., and Ultragenyx Pharmaceutical Inc.

Polaris Market Research has segmented the market report on the basis of disease type, type of therapy, end user, and region:

By Disease Type Outlook (Revenue, USD Billion, 2020-2034)

Gaucher's Diseases

Fabry Diseases

Pompe's Syndrome

Mucopolysaccharidosis

Others

By Type of Therapy Outlook (Revenue, USD Billion, 2020-2034)

Enzyme Replacement Therapy

Stem Cell Therapy

Substrate Reduction Therapy

Others

By End User Outlook (Revenue, USD Billion, 2020-2034)

Hospitals

Clinics

Others

By Regional Outlook (Revenue, USD Billion, 2020-2034)

North America

US

Canada

Europe

Germany

France

UK

Italy

Spain

Netherlands

Russia

Rest of Europe

Asia Pacific

China

Japan

India

Malaysia

South Korea

Indonesia

Australia

Vietnam

Rest of Asia Pacific

Middle East & Africa

Saudi Arabia

UAE

Israel

South Africa

Rest of Middle East & Africa

Latin America

Mexico

Brazil

Argentina

Rest of Latin America

Table of Contents

1. Introduction

  • 1.1. Report Description
    • 1.1.1. Objectives of the Study
    • 1.1.2. Market Scope
    • 1.1.3. Assumptions
  • 1.2. Stakeholders

2. Executive Summary

  • 2.1. Market Highlights

3. Research Methodology

  • 3.1. Overview
    • 3.1.1. Data Mining
  • 3.2. Data Sources
    • 3.2.1. Primary Sources
    • 3.2.2. Secondary Sources

4. Global Lysosomal Storage Disease Treatment Market Insights

  • 4.1. Lysosomal Storage Disease Treatment Market - Market Snapshot
  • 4.2. Lysosomal Storage Disease Treatment Market Dynamics
    • 4.2.1. Drivers and Opportunities
      • 4.2.1.1. Rising Incidence of Rare Genetic Disorders
      • 4.2.1.2. Advancements in Enzyme Replacement Therapy (ERT)
    • 4.2.2. Restraints and Challenges
      • 4.2.2.1. High Treatment Costs and Limited Reimbursement
  • 4.3. Porter's Five Forces Analysis
    • 4.3.1. Bargaining Power of Suppliers (Moderate)
    • 4.3.2. Threats of New Entrants: (Low)
    • 4.3.3. Bargaining Power of Buyers (Moderate)
    • 4.3.4. Threat of Substitute (Moderate)
    • 4.3.5. Rivalry among existing firms (High)
  • 4.4. PESTEL Analysis
  • 4.5. Lysosomal Storage Disease Treatment Market Trends
  • 4.6. Value Chain Analysis

5. Global Lysosomal Storage Disease Treatment Market, by Disease Type

  • 5.1. Key Findings
  • 5.2. Introduction
    • 5.2.1. Global Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
  • 5.3. Gaucher's Diseases
    • 5.3.1. Global Lysosomal Storage Disease Treatment Market, by Gaucher's Diseases, by Region, 2020-2034 (USD Billion)
  • 5.4. Fabry Diseases
    • 5.4.1. Global Lysosomal Storage Disease Treatment Market, by Fabry Diseases, by Region, 2020-2034 (USD Billion)
  • 5.5. Pompe's Syndrome
    • 5.5.1. Global Lysosomal Storage Disease Treatment Market, by Pompe's Syndrome, by Region, 2020-2034 (USD Billion)
  • 5.6. Mucopolysaccharidosis
    • 5.6.1. Global Lysosomal Storage Disease Treatment Market, by Mucopolysaccharidosis, by Region, 2020-2034 (USD Billion)
  • 5.7. Others
    • 5.7.1. Global Lysosomal Storage Disease Treatment Market, by Others, by Region, 2020-2034 (USD Billion)

6. Global Lysosomal Storage Disease Treatment Market, by Type of Therapy

  • 6.1. Key Findings
  • 6.2. Introduction
    • 6.2.1. Global Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
  • 6.3. Enzyme Replacement Therapy
    • 6.3.1. Global Lysosomal Storage Disease Treatment Market, by Enzyme Replacement Therapy, by Region, 2020-2034 (USD Billion)
  • 6.4. Stem Cell Therapy
    • 6.4.1. Global Lysosomal Storage Disease Treatment Market, by Stem Cell Therapy, by Region, 2020-2034 (USD Billion)
  • 6.5. Substrate Reduction Therapy
    • 6.5.1. Global Lysosomal Storage Disease Treatment Market, by Substrate Reduction Therapy, by Region, 2020-2034 (USD Billion)
  • 6.6. Others
    • 6.6.1. Global Lysosomal Storage Disease Treatment Market, by Others, by Region, 2020-2034 (USD Billion)

7. Global Lysosomal Storage Disease Treatment Market, by End User

  • 7.1. Key Findings
  • 7.2. Introduction
    • 7.2.1. Global Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
  • 7.3. Hospitals
    • 7.3.1. Global Lysosomal Storage Disease Treatment Market, by Hospitals, by Region, 2020-2034 (USD Billion)
  • 7.4. Clinics
    • 7.4.1. Global Lysosomal Storage Disease Treatment Market, by Clinics, by Region, 2020-2034 (USD Billion)
  • 7.5. Others
    • 7.5.1. Global Lysosomal Storage Disease Treatment Market, by Others, by Region, 2020-2034 (USD Billion)

8. Global Lysosomal Storage Disease Treatment Market, by Geography

  • 8.1. Key Findings
  • 8.2. Introduction
    • 8.2.1. Lysosomal Storage Disease Treatment Market Assessment, By Geography, 2020-2034 (USD Billion)
  • 8.3. Lysosomal Storage Disease Treatment Market - North America
    • 8.3.1. North America: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
    • 8.3.2. North America: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
    • 8.3.3. North America: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
    • 8.3.4. Lysosomal Storage Disease Treatment Market - U.S.
      • 8.3.4.1. U.S.: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
      • 8.3.4.2. U.S.: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
      • 8.3.4.3. U.S.: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
    • 8.3.5. Lysosomal Storage Disease Treatment Market - Canada
      • 8.3.5.1. Canada: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
      • 8.3.5.2. Canada: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
      • 8.3.5.3. Canada: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
  • 8.4. Lysosomal Storage Disease Treatment Market - Europe
    • 8.4.1. Europe: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
    • 8.4.2. Europe: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
    • 8.4.3. Europe: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
    • 8.4.4. Lysosomal Storage Disease Treatment Market - UK
      • 8.4.4.1. UK: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
      • 8.4.4.2. UK: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
      • 8.4.4.3. UK: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
    • 8.4.5. Lysosomal Storage Disease Treatment Market - France
      • 8.4.5.1. France: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
      • 8.4.5.2. France: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
      • 8.4.5.3. France: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
    • 8.4.6. Lysosomal Storage Disease Treatment Market - Germany
      • 8.4.6.1. Germany: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
      • 8.4.6.2. Germany: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
      • 8.4.6.3. Germany: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
    • 8.4.7. Lysosomal Storage Disease Treatment Market - Italy
      • 8.4.7.1. Italy: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
      • 8.4.7.2. Italy: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
      • 8.4.7.3. Italy: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
    • 8.4.8. Lysosomal Storage Disease Treatment Market - Spain
      • 8.4.8.1. Spain: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
      • 8.4.8.2. Spain: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
      • 8.4.8.3. Spain: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
    • 8.4.9. Lysosomal Storage Disease Treatment Market - Netherlands
      • 8.4.9.1. Netherlands: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
      • 8.4.9.2. Netherlands: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
      • 8.4.9.3. Netherlands: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
    • 8.4.10. Lysosomal Storage Disease Treatment Market - Russia
      • 8.4.10.1. Russia: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
      • 8.4.10.2. Russia: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
      • 8.4.10.3. Russia: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
    • 8.4.11. Lysosomal Storage Disease Treatment Market - Rest of Europe
      • 8.4.11.1. Rest of Europe: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
      • 8.4.11.2. Rest of Europe: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
      • 8.4.11.3. Rest of Europe: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
  • 8.5. Lysosomal Storage Disease Treatment Market - Asia Pacific
    • 8.5.1. Asia Pacific: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
    • 8.5.2. Asia Pacific: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
    • 8.5.3. Asia Pacific: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
    • 8.5.4. Lysosomal Storage Disease Treatment Market - China
      • 8.5.4.1. China: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
      • 8.5.4.2. China: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
      • 8.5.4.3. China: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
    • 8.5.5. Lysosomal Storage Disease Treatment Market - India
      • 8.5.5.1. India: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
      • 8.5.5.2. India: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
      • 8.5.5.3. India: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
    • 8.5.6. Lysosomal Storage Disease Treatment Market - Malaysia
      • 8.5.6.1. Malaysia: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
      • 8.5.6.2. Malaysia: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
      • 8.5.6.3. Malaysia: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
    • 8.5.7. Lysosomal Storage Disease Treatment Market - Japan
      • 8.5.7.1. Japan: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
      • 8.5.7.2. Japan: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
      • 8.5.7.3. Japan: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
    • 8.5.8. Lysosomal Storage Disease Treatment Market - Indonesia
      • 8.5.8.1. Indonesia: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
      • 8.5.8.2. Indonesia: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
      • 8.5.8.3. Indonesia: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
    • 8.5.9. Lysosomal Storage Disease Treatment Market - South Korea
      • 8.5.9.1. South Korea: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
      • 8.5.9.2. South Korea: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
      • 8.5.9.3. South Korea: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
    • 8.5.10. Lysosomal Storage Disease Treatment Market - Australia
      • 8.5.10.1. Australia: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
      • 8.5.10.2. Australia: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
      • 8.5.10.3. Australia: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
    • 8.5.11. Lysosomal Storage Disease Treatment Market - Rest of Asia Pacific
      • 8.5.11.1. Rest of Asia Pacific: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
      • 8.5.11.2. Rest of Asia Pacific: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
      • 8.5.11.3. Rest of Asia Pacific: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
  • 8.6. Lysosomal Storage Disease Treatment Market - Middle East & Africa
    • 8.6.1. Middle East & Africa: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
    • 8.6.2. Middle East & Africa: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
    • 8.6.3. Middle East & Africa: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
    • 8.6.4. Lysosomal Storage Disease Treatment Market - Saudi Arabia
      • 8.6.4.1. Saudi Arabia: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
      • 8.6.4.2. Saudi Arabia: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
      • 8.6.4.3. Saudi Arabia: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
    • 8.6.5. Lysosomal Storage Disease Treatment Market - UAE
      • 8.6.5.1. UAE: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
      • 8.6.5.2. UAE: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
      • 8.6.5.3. UAE: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
    • 8.6.6. Lysosomal Storage Disease Treatment Market - Israel
      • 8.6.6.1. Israel: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
      • 8.6.6.2. Israel: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
      • 8.6.6.3. Israel: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
    • 8.6.7. Lysosomal Storage Disease Treatment Market - South Africa
      • 8.6.7.1. South Africa: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
      • 8.6.7.2. South Africa: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
      • 8.6.7.3. South Africa: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
    • 8.6.8. Lysosomal Storage Disease Treatment Market - Rest of Middle East & Africa
      • 8.6.8.1. Rest of Middle East & Africa: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
      • 8.6.8.2. Rest of Middle East & Africa: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
      • 8.6.8.3. Rest of Middle East & Africa: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
  • 8.7. Lysosomal Storage Disease Treatment Market - Latin America
    • 8.7.1. Latin America: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
    • 8.7.2. Latin America: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
    • 8.7.3. Latin America: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
    • 8.7.4. Lysosomal Storage Disease Treatment Market - Mexico
      • 8.7.4.1. Mexico: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
      • 8.7.4.2. Mexico: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
      • 8.7.4.3. Mexico: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
    • 8.7.5. Lysosomal Storage Disease Treatment Market - Brazil
      • 8.7.5.1. Brazil: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
      • 8.7.5.2. Brazil: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
      • 8.7.5.3. Brazil: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
    • 8.7.6. Lysosomal Storage Disease Treatment Market - Argentina
      • 8.7.6.1. Argentina: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
      • 8.7.6.2. Argentina: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
      • 8.7.6.3. Argentina: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
    • 8.7.7. Lysosomal Storage Disease Treatment Market - Rest of Latin America
      • 8.7.7.1. Rest of Latin America: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
      • 8.7.7.2. Rest of Latin America: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
      • 8.7.7.3. Rest of Latin America: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)

9. Competitive Landscape

  • 9.1. Expansion and Acquisition Analysis
    • 9.1.1. Expansion
    • 9.1.2. Acquisitions
  • 9.2. Partnerships/Collaborations/Agreements/Exhibitions

10. Company Profiles

  • 10.1. Alexion Pharmaceuticals, Inc.
    • 10.1.1. Company Overview
    • 10.1.2. Financial Performance
    • 10.1.3. Disease Type Benchmarking
    • 10.1.4. Recent Development
  • 10.2. Amicus Therapeutics, Inc.
    • 10.2.1. Company Overview
    • 10.2.2. Financial Performance
    • 10.2.3. Disease Type Benchmarking
    • 10.2.4. Recent Development
  • 10.3. BioMarin Pharmaceutical Inc.
    • 10.3.1. Company Overview
    • 10.3.2. Financial Performance
    • 10.3.3. Disease Type Benchmarking
    • 10.3.4. Recent Development
  • 10.4. Eli Lilly and Company
    • 10.4.1. Company Overview
    • 10.4.2. Financial Performance
    • 10.4.3. Disease Type Benchmarking
    • 10.4.4. Recent Development
  • 10.5. Johnson & Johnson (Actelion Pharmaceuticals Ltd.)
    • 10.5.1. Company Overview
    • 10.5.2. Financial Performance
    • 10.5.3. Disease Type Benchmarking
    • 10.5.4. Recent Development
  • 10.6. Merck & Co., Inc.
    • 10.6.1. Company Overview
    • 10.6.2. Financial Performance
    • 10.6.3. Disease Type Benchmarking
    • 10.6.4. Recent Development
  • 10.7. Novartis AG
    • 10.7.1. Company Overview
    • 10.7.2. Financial Performance
    • 10.7.3. Disease Type Benchmarking
    • 10.7.4. Recent Development
  • 10.8. Pfizer Inc.
    • 10.8.1. Company Overview
    • 10.8.2. Financial Performance
    • 10.8.3. Disease Type Benchmarking
    • 10.8.4. Recent Development
  • 10.9. Sanofi (Genzyme Corporation)
    • 10.9.1. Company Overview
    • 10.9.2. Financial Performance
    • 10.9.3. Disease Type Benchmarking
    • 10.9.4. Recent Development
  • 10.10. Sigilon Therapeutics, Inc.
    • 10.10.1. Company Overview
    • 10.10.2. Financial Performance
    • 10.10.3. Disease Type Benchmarking
    • 10.10.4. Recent Development
  • 10.11. Takeda Pharmaceutical Company Limited (Shire Plc)
    • 10.11.1. Company Overview
    • 10.11.2. Financial Performance
    • 10.11.3. Disease Type Benchmarking
    • 10.11.4. Recent Development
  • 10.12. Chiesi Farmaceutici S.p.A.
    • 10.12.1. Company Overview
    • 10.12.2. Financial Performance
    • 10.12.3. Disease Type Benchmarking
    • 10.12.4. Recent Development

List of Tables:

  • Table 1 Global Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
  • Table 2 Global Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
  • Table 3 Global Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
  • Table 4 North America: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
  • Table 5 North America: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
  • Table 6 North America: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
  • Table 7 U.S.: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
  • Table 8 U.S.: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
  • Table 9 U.S.: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
  • Table 10 Canada: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
  • Table 11 Canada: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
  • Table 12 Canada: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
  • Table 13 Europe: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
  • Table 14 Europe: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
  • Table 15 Europe: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
  • Table 16 UK: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
  • Table 17 UK: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
  • Table 18 UK: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
  • Table 19 France: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
  • Table 20 France: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
  • Table 21 France: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
  • Table 22 Germany: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
  • Table 23 Germany: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
  • Table 24 Germany: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
  • Table 25 Italy: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
  • Table 26 Italy: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
  • Table 27 Italy: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
  • Table 28 Spain: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
  • Table 29 Spain: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
  • Table 30 Spain: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
  • Table 31 Netherlands: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
  • Table 32 Netherlands: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
  • Table 33 Netherlands: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
  • Table 34 Russia: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
  • Table 35 Russia: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
  • Table 36 Russia: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
  • Table 37 Rest of Europe: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
  • Table 38 Rest of Europe: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
  • Table 39 Rest of Europe: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
  • Table 40 Asia Pacific: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
  • Table 41 Asia Pacific: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
  • Table 42 Asia Pacific: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
  • Table 43 China: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
  • Table 44 China: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
  • Table 45 China: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
  • Table 46 India: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
  • Table 47 India: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
  • Table 48 India: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
  • Table 49 Malaysia: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
  • Table 50 Malaysia: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
  • Table 51 Malaysia: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
  • Table 52 Japan: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
  • Table 53 Japan: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
  • Table 54 Japan: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
  • Table 55 Indonesia: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
  • Table 56 Indonesia: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
  • Table 57 Indonesia: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
  • Table 58 South Korea: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
  • Table 59 South Korea: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
  • Table 60 South Korea: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
  • Table 61 Australia: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
  • Table 62 Australia: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
  • Table 63 Australia: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
  • Table 64 Rest of Asia Pacific: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
  • Table 65 Rest of Asia Pacific: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
  • Table 66 Rest of Asia Pacific: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
  • Table 67 Middle East & Africa: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
  • Table 68 Middle East & Africa: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
  • Table 69 Middle East & Africa: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
  • Table 70 Saudi Arabia: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
  • Table 71 Saudi Arabia: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
  • Table 72 Saudi Arabia: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
  • Table 73 UAE: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
  • Table 74 UAE: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
  • Table 75 UAE: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
  • Table 76 Israel: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
  • Table 77 Israel: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
  • Table 78 Israel: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
  • Table 79 South Africa: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
  • Table 80 South Africa: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
  • Table 81 South Africa: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
  • Table 82 Rest of Middle East & Africa: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
  • Table 83 Rest of Middle East & Africa: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
  • Table 84 Rest of Middle East & Africa: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
  • Table 85 Latin America: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
  • Table 86 Latin America: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
  • Table 87 Latin America: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
  • Table 88 Mexico: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
  • Table 89 Mexico: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
  • Table 90 Mexico: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
  • Table 91 Brazil: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
  • Table 92 Brazil: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
  • Table 93 Brazil: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
  • Table 94 Argentina: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
  • Table 95 Argentina: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
  • Table 96 Argentina: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
  • Table 97 Rest of Latin America: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
  • Table 98 Rest of Latin America: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
  • Table 99 Rest of Latin America: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)

List of Figures:

  • Figure 1. Global Lysosomal Storage Disease Treatment Market, 2020-2034 (USD Billion)
  • Figure 2. Integrated Ecosystem
  • Figure 3. Research Methodology: Top-Down & Bottom-Up Price
  • Figure 4. Market by Geography
  • Figure 5. Porter's Five Forces
  • Figure 6. Market by Disease Type
  • Figure 7. Global Lysosomal Storage Disease Treatment Market, by Disease Type, 2024 & 2034 (USD Billion)
  • Figure 8. Market by Type of Therapy
  • Figure 9. Global Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2024 & 2034 (USD Billion)
  • Figure 10. Market by End User
  • Figure 11. Global Lysosomal Storage Disease Treatment Market, by End User, 2024 & 2034 (USD Billion)
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