地中海貧血治療市場－全球產業規模、佔有率、趨勢、機會和預測（按治療、類型、最終用戶、地區和競爭細分，2020-2030 年）

2024 年全球地中海貧血治療市場價值為 9.0105 億美元，預計到 2030 年將達到 14.192 億美元，預測期內複合年成長率為 7.84%。市場正在經歷一場轉型，推動力包括診斷率的提高、醫療保健服務的改善以及公共和私人部門為治療罕見遺傳疾病所做的努力的不斷擴大。患者和醫療保健提供者的意識增強有助於早期篩檢和及時干預。雖然輸血仍然是核心治療方式，但螯合療法的進步已經提高了長期安全性和治療效果。製藥公司正在積極開發像luspatercept和mitapivat這樣的療法，以減少輸血依賴並增加血紅素的生成。同時，新興市場正在加強規範輸血服務的基礎設施，促進更廣泛地採用綜合護理模式，並推動全球市場成長。

關鍵市場促進因素

全球地中海貧血盛行率上升

主要市場挑戰

獲得先進療法的機會有限

主要市場趨勢

基因編輯療法的出現

目錄

第 1 章：產品概述

第2章：研究方法

第3章：執行摘要

第4章：顧客之聲

第5章：全球地中海貧血治療市場展望

• 市場規模和預測
  • 按價值
• 市場佔有率和預測
  • 依治療方法（鐵螯合藥物、輸血、紅血球成熟劑、幹細胞療法等）
  • 依類型（α地中海貧血、BETA地中海貧血）
  • 按最終使用者（醫院、研究機構、其他）
  • 按公司分類（2024）
  • 按地區
• 市場地圖

第6章：北美地中海貧血治療市場展望

• 市場規模和預測
• 市場佔有率和預測
• 北美：國家分析
  • 美國
  • 墨西哥
  • 加拿大

第7章：歐洲地中海貧血治療市場展望

• 市場規模和預測
• 市場佔有率和預測
• 歐洲：國家分析
  • 法國
  • 德國
  • 英國
  • 義大利
  • 西班牙

第8章：亞太地區地中海貧血治療市場展望

• 市場規模和預測
• 市場佔有率和預測
• 亞太地區：國家分析
  • 中國
  • 印度
  • 韓國
  • 日本
  • 澳洲

第9章：南美洲地中海貧血治療市場展望

• 市場規模和預測
• 市場佔有率和預測
• 南美洲：國家分析
  • 巴西
  • 阿根廷
  • 哥倫比亞

第10章：中東與非洲地中海貧血治療市場展望

• 市場規模和預測
• 市場佔有率和預測
• MEA：國家分析
  • 南非
  • 沙烏地阿拉伯
  • 阿拉伯聯合大公國

第 11 章：市場動態

• 驅動程式
• 挑戰

第 12 章：市場趨勢與發展

• 合併與收購（如有）
• 產品發布（如有）
• 最新動態

第 13 章：波特五力分析

• 產業競爭
• 新進入者的潛力
• 供應商的力量
• 顧客的力量
• 替代產品的威脅

第 14 章：競爭格局

• Bluebird Bio, Inc.
• Merck & Co., Inc.
• Novartis AG
• ApoPharma Inc.
• Pfizer, Inc.
• Celgene Corporation
• Takeda Pharmaceuticals Company Limited
• Incyte Corporation
• Bellicum Pharmaceuticals
• GSK plc

第 15 章：策略建議

第16章調查會社について,免責事項

The Global Thalassemia Treatment Market was valued at USD 901.05 Million in 2024 and is projected to reach USD 1,419.20 Million by 2030, growing at a CAGR of 7.84% during the forecast period. The market is undergoing a transformation driven by increasing diagnosis rates, improved healthcare access, and expanding public and private efforts to manage rare genetic disorders. Enhanced awareness among patients and healthcare providers is encouraging early screening and timely intervention. While blood transfusions remain a core treatment modality, advancements in chelation therapies have improved long-term safety and outcomes. Pharmaceutical companies are actively developing therapies like luspatercept and mitapivat to reduce transfusion dependency and increase hemoglobin production. Simultaneously, emerging markets are enhancing infrastructure for regulated transfusion services, contributing to a broader adoption of comprehensive care models and fueling global market growth.

Key Market Drivers

Rising Global Prevalence of Thalassemia

The growing global prevalence of thalassemia is a major driver of market expansion. Thalassemia, a genetic blood disorder, is most prevalent in regions such as Southeast Asia, the Mediterranean, the Middle East, and North Africa. According to the World Health Organization (WHO), approximately 5% of the global population carries the thalassemia gene, contributing to increasing case numbers, especially in areas lacking genetic counseling or prenatal screening. As diagnosis rates improve, demand for lifelong care-including regular transfusions and iron chelation therapy-is rising. In parallel, innovative treatments such as stem cell transplantation and gene therapy are gaining attention as potential curative options. Governments and health organizations are investing in early detection programs, public health campaigns, and treatment facilities, all of which are fueling sustained market growth by ensuring better access to thalassemia care.

Key Market Challenges

Limited Access to Advanced Therapies

A significant challenge facing the thalassemia treatment market is the limited access to advanced therapies, particularly in low- and middle-income regions. While gene therapies and stem cell transplants offer promising long-term outcomes or potential cures, their availability is often restricted due to high costs, complex infrastructure requirements, and the need for specialized medical expertise. These therapies are financially inaccessible for many patients, with prices often reaching hundreds of thousands of dollars. Moreover, resource-poor regions lack the necessary facilities and personnel to support advanced treatments, leaving patients dependent on traditional methods like blood transfusions and iron chelation, which are less effective over the long term. This disparity in care contributes to uneven patient outcomes and underscores the need for global strategies to improve accessibility, affordability, and infrastructure for advanced thalassemia therapies.

Key Market Trends

Emergence of Gene Editing Therapies

Gene editing therapies, particularly CRISPR-Cas9, are emerging as transformative innovations in the treatment of thalassemia. These techniques allow precise modification of defective genes responsible for the disease, offering the potential for a one-time curative approach. Traditional therapies manage symptoms without addressing the genetic root cause, whereas gene editing targets and corrects the underlying mutation. In 2023, clinical trials showed positive outcomes using CRISPR-Cas9 to treat beta-thalassemia, significantly reducing or eliminating transfusion needs. Companies like CRISPR Therapeutics and Vertex Pharmaceuticals are advancing therapies such as CTX001, which modifies patient stem cells to promote functional hemoglobin production. These advancements mark a shift toward personalized, curative treatments that could redefine long-term disease management. As regulatory pathways for orphan drugs and genetic therapies evolve, these approaches are expected to play a larger role in the future of thalassemia care.

Key Market Players

• Bluebird Bio, Inc.
• Merck & Co., Inc.
• Novartis AG
• ApoPharma Inc.
• Pfizer, Inc.
• Celgene Corporation
• Takeda Pharmaceuticals Company Limited
• Incyte Corporation
• Bellicum Pharmaceuticals
• GSK plc

Report Scope

In this report, the Global Thalassemia Treatment Market has been segmented into the following categories, in addition to the industry trends which have also been detailed below:

Thalassemia Treatment Market, By Treatment:

• Iron Chelating Drugs
• Blood Transfusions
• Erythyroid Maturation Agents
• Stem Cell Therapy
• Others

Thalassemia Treatment Market, By Type:

• Alpha Thalassemia
• Beta Thalassemia

Thalassemia Treatment Market, By End User:

• Hospitals
• Research Institutes
• Others

Thalassemia Treatment Market, By Region:

• North America
  • United States
  • Canada
  • Mexico
• Europe
  • France
  • United Kingdom
  • Italy
  • Germany
  • Spain
• Asia-Pacific
  • China
  • India
  • Japan
  • Australia
  • South Korea
• South America
  • Brazil
  • Argentina
  • Colombia
• Middle East & Africa
  • South Africa
  • Saudi Arabia
  • UAE

Competitive Landscape

Company Profiles: Detailed analysis of the major companies present in the Global Thalassemia Treatment Market.

Available Customizations

Global Thalassemia Treatment Market report with the given market data, TechSci Research offers customizations according to a company's specific needs. The following customization options are available for the report:

Company Information

• Detailed analysis and profiling of additional market players (up to five).

Table of Contents

1. Product Overview

• 1.1. Market Definition
• 1.2. Scope of the Market
  • 1.2.1. Markets Covered
  • 1.2.2. Years Considered for Study
  • 1.2.3. Key Market Segmentations

2. Research Methodology

• 2.1. Objective of the Study
• 2.2. Baseline Methodology
• 2.3. Key Industry Partners
• 2.4. Major Association and Secondary Sources
• 2.5. Forecasting Methodology
• 2.6. Data Triangulation & Validation
• 2.7. Assumptions and Limitations

3. Executive Summary

• 3.1. Overview of the Market
• 3.2. Overview of Key Market Segmentations
• 3.3. Overview of Key Market Players
• 3.4. Overview of Key Regions/Countries
• 3.5. Overview of Market Drivers, Challenges, and Trends

4. Voice of Customer

5. Global Thalassemia Treatment Market Outlook

• 5.1. Market Size & Forecast
  • 5.1.1. By Value
• 5.2. Market Share & Forecast
  • 5.2.1. By Treatment (Iron Chelating Drugs, Blood Transfusions, Erythyroid Maturation Agents, Stem Cell Therapy, Others)
  • 5.2.2. By Type (Alpha Thalassemia, Beta Thalassemia)
  • 5.2.3. By End User (Hospitals, Research Institutes, Others)
  • 5.2.4. By Company (2024)
  • 5.2.5. By Region
• 5.3. Market Map

6. North America Thalassemia Treatment Market Outlook

• 6.1. Market Size & Forecast
  • 6.1.1. By Value
• 6.2. Market Share & Forecast
  • 6.2.1. By Treatment
  • 6.2.2. By Type
  • 6.2.3. By End User
  • 6.2.4. By Country
• 6.3. North America: Country Analysis
  • 6.3.1. United States Thalassemia Treatment Market Outlook
    • 6.3.1.1. Market Size & Forecast
      • 6.3.1.1.1. By Value
    • 6.3.1.2. Market Share & Forecast
      • 6.3.1.2.1. By Treatment
      • 6.3.1.2.2. By Type
      • 6.3.1.2.3. By End User
  • 6.3.2. Mexico Thalassemia Treatment Market Outlook
    • 6.3.2.1. Market Size & Forecast
      • 6.3.2.1.1. By Value
    • 6.3.2.2. Market Share & Forecast
      • 6.3.2.2.1. By Treatment
      • 6.3.2.2.2. By Type
      • 6.3.2.2.3. By End User
  • 6.3.3. Canada Thalassemia Treatment Market Outlook
    • 6.3.3.1. Market Size & Forecast
      • 6.3.3.1.1. By Value
    • 6.3.3.2. Market Share & Forecast
      • 6.3.3.2.1. By Treatment
      • 6.3.3.2.2. By Type
      • 6.3.3.2.3. By End User

7. Europe Thalassemia Treatment Market Outlook

• 7.1. Market Size & Forecast
  • 7.1.1. By Value
• 7.2. Market Share & Forecast
  • 7.2.1. By Treatment
  • 7.2.2. By Type
  • 7.2.3. By End User
  • 7.2.4. By Country
• 7.3. Europe: Country Analysis
  • 7.3.1. France Thalassemia Treatment Market Outlook
    • 7.3.1.1. Market Size & Forecast
      • 7.3.1.1.1. By Value
    • 7.3.1.2. Market Share & Forecast
      • 7.3.1.2.1. By Treatment
      • 7.3.1.2.2. By Type
      • 7.3.1.2.3. By End User
  • 7.3.2. Germany Thalassemia Treatment Market Outlook
    • 7.3.2.1. Market Size & Forecast
      • 7.3.2.1.1. By Value
    • 7.3.2.2. Market Share & Forecast
      • 7.3.2.2.1. By Treatment
      • 7.3.2.2.2. By Type
      • 7.3.2.2.3. By End User
  • 7.3.3. United Kingdom Thalassemia Treatment Market Outlook
    • 7.3.3.1. Market Size & Forecast
      • 7.3.3.1.1. By Value
    • 7.3.3.2. Market Share & Forecast
      • 7.3.3.2.1. By Treatment
      • 7.3.3.2.2. By Type
      • 7.3.3.2.3. By End User
  • 7.3.4. Italy Thalassemia Treatment Market Outlook
    • 7.3.4.1. Market Size & Forecast
      • 7.3.4.1.1. By Value
    • 7.3.4.2. Market Share & Forecast
      • 7.3.4.2.1. By Treatment
      • 7.3.4.2.2. By Type
      • 7.3.4.2.3. By End User
  • 7.3.5. Spain Thalassemia Treatment Market Outlook
    • 7.3.5.1. Market Size & Forecast
      • 7.3.5.1.1. By Value
    • 7.3.5.2. Market Share & Forecast
      • 7.3.5.2.1. By Treatment
      • 7.3.5.2.2. By Type
      • 7.3.5.2.3. By End User

8. Asia-Pacific Thalassemia Treatment Market Outlook

• 8.1. Market Size & Forecast
  • 8.1.1. By Value
• 8.2. Market Share & Forecast
  • 8.2.1. By Treatment
  • 8.2.2. By Type
  • 8.2.3. By End User
  • 8.2.4. By Country
• 8.3. Asia-Pacific: Country Analysis
  • 8.3.1. China Thalassemia Treatment Market Outlook
    • 8.3.1.1. Market Size & Forecast
      • 8.3.1.1.1. By Value
    • 8.3.1.2. Market Share & Forecast
      • 8.3.1.2.1. By Treatment
      • 8.3.1.2.2. By Type
      • 8.3.1.2.3. By End User
  • 8.3.2. India Thalassemia Treatment Market Outlook
    • 8.3.2.1. Market Size & Forecast
      • 8.3.2.1.1. By Value
    • 8.3.2.2. Market Share & Forecast
      • 8.3.2.2.1. By Treatment
      • 8.3.2.2.2. By Type
      • 8.3.2.2.3. By End User
  • 8.3.3. South Korea Thalassemia Treatment Market Outlook
    • 8.3.3.1. Market Size & Forecast
      • 8.3.3.1.1. By Value
    • 8.3.3.2. Market Share & Forecast
      • 8.3.3.2.1. By Treatment
      • 8.3.3.2.2. By Type
      • 8.3.3.2.3. By End User
  • 8.3.4. Japan Thalassemia Treatment Market Outlook
    • 8.3.4.1. Market Size & Forecast
      • 8.3.4.1.1. By Value
    • 8.3.4.2. Market Share & Forecast
      • 8.3.4.2.1. By Treatment
      • 8.3.4.2.2. By Type
      • 8.3.4.2.3. By End User
  • 8.3.5. Australia Thalassemia Treatment Market Outlook
    • 8.3.5.1. Market Size & Forecast
      • 8.3.5.1.1. By Value
    • 8.3.5.2. Market Share & Forecast
      • 8.3.5.2.1. By Treatment
      • 8.3.5.2.2. By Type
      • 8.3.5.2.3. By End User

9. South America Thalassemia Treatment Market Outlook

• 9.1. Market Size & Forecast
  • 9.1.1. By Value
• 9.2. Market Share & Forecast
  • 9.2.1. By Treatment
  • 9.2.2. By Type
  • 9.2.3. By End User
  • 9.2.4. By Country
• 9.3. South America: Country Analysis
  • 9.3.1. Brazil Thalassemia Treatment Market Outlook
    • 9.3.1.1. Market Size & Forecast
      • 9.3.1.1.1. By Value
    • 9.3.1.2. Market Share & Forecast
      • 9.3.1.2.1. By Treatment
      • 9.3.1.2.2. By Type
      • 9.3.1.2.3. By End User
  • 9.3.2. Argentina Thalassemia Treatment Market Outlook
    • 9.3.2.1. Market Size & Forecast
      • 9.3.2.1.1. By Value
    • 9.3.2.2. Market Share & Forecast
      • 9.3.2.2.1. By Treatment
      • 9.3.2.2.2. By Type
      • 9.3.2.2.3. By End User
  • 9.3.3. Colombia Thalassemia Treatment Market Outlook
    • 9.3.3.1. Market Size & Forecast
      • 9.3.3.1.1. By Value
    • 9.3.3.2. Market Share & Forecast
      • 9.3.3.2.1. By Treatment
      • 9.3.3.2.2. By Type
      • 9.3.3.2.3. By End User

10. Middle East and Africa Thalassemia Treatment Market Outlook

• 10.1. Market Size & Forecast
  • 10.1.1. By Value
• 10.2. Market Share & Forecast
  • 10.2.1. By Treatment
  • 10.2.2. By Type
  • 10.2.3. By End User
  • 10.2.4. By Country
• 10.3. MEA: Country Analysis
  • 10.3.1. South Africa Thalassemia Treatment Market Outlook
    • 10.3.1.1. Market Size & Forecast
      • 10.3.1.1.1. By Value
    • 10.3.1.2. Market Share & Forecast
      • 10.3.1.2.1. By Treatment
      • 10.3.1.2.2. By Type
      • 10.3.1.2.3. By End User
  • 10.3.2. Saudi Arabia Thalassemia Treatment Market Outlook
    • 10.3.2.1. Market Size & Forecast
      • 10.3.2.1.1. By Value
    • 10.3.2.2. Market Share & Forecast
      • 10.3.2.2.1. By Treatment
      • 10.3.2.2.2. By Type
      • 10.3.2.2.3. By End User
  • 10.3.3. UAE Thalassemia Treatment Market Outlook
    • 10.3.3.1. Market Size & Forecast
      • 10.3.3.1.1. By Value
    • 10.3.3.2. Market Share & Forecast
      • 10.3.3.2.1. By Treatment
      • 10.3.3.2.2. By Type
      • 10.3.3.2.3. By End User

11. Market Dynamics

• 11.1. Drivers
• 11.2. Challenges

12. Market Trends & Developments

• 12.1. Merger & Acquisition (If Any)
• 12.2. Product Launches (If Any)
• 12.3. Recent Developments

13. Porters Five Forces Analysis

• 13.1. Competition in the Industry
• 13.2. Potential of New Entrants
• 13.3. Power of Suppliers
• 13.4. Power of Customers
• 13.5. Threat of Substitute Products

14. Competitive Landscape

• 14.1. Bluebird Bio, Inc.
  • 14.1.1. Business Overview
  • 14.1.2. Company Snapshot
  • 14.1.3. Products & Services
  • 14.1.4. Financials (As Reported)
  • 14.1.5. Recent Developments
  • 14.1.6. Key Personnel Details
  • 14.1.7. SWOT Analysis
• 14.2. Merck & Co., Inc.
• 14.3. Novartis AG
• 14.4. ApoPharma Inc.
• 14.5. Pfizer, Inc.
• 14.6. Celgene Corporation
• 14.7. Takeda Pharmaceuticals Company Limited
• 14.8. Incyte Corporation
• 14.9. Bellicum Pharmaceuticals
• 14.10. GSK plc

15. Strategic Recommendations

16. About Us & Disclaimer